alyaza [they/she] ( alyaza@beehaw.org ) MA to

ScienceEnglish · 3 years ago

First gene therapy for deadly form of muscular dystrophy gets FDA approval for young children

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First gene therapy for deadly form of muscular dystrophy gets FDA approval for young children

alyaza [they/she] ( alyaza@beehaw.org ) MA to

ScienceEnglish · 3 years ago

5

The treatment from Sarepta Therapeutics was approved Thursday for children ages 4 and 5 with Duchenne muscular dystrophy, a rare muscle-wasting disease that causes early death.

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anji ( anji@lemmy.anji.nl )
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3 years ago
I hope it really works. Muscular dystrophy is such a bag of dicks. Poor kids.

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